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Director, Health Economics & Outcomes Research, Achondroplasia

Location London, United Kingdom

BioMarin is the world leader in delivering therapeutics that provide meaningful advances to patients who live with serious and life-threatening rare genetic diseases. We target diseases that lack effective therapies and affect relatively small numbers of patients, many of whom are children. These conditions are often inherited, difficult to diagnose, progressively debilitating and have few, if any, treatment options. BioMarin will continue to focus on advancing therapies that are the first or best of their kind.

BioMarin’s Commercial organization supports our global sales and marketing efforts around the world. Our global sales force continues to solidify the company’s commercial presence in the United States and Europe and is rapidly growing in other regions, such as Latin America, the Middle East and Asia-Pacific. Come join our team and make a meaningful impact on patients’ lives.


This role will focuson developing the value argumentation and payer evidence strategy and execution for BioMarins marketed and pipeline programs, specifically BioMarins achondroplasia treatment VOXZOGO (vosoritide).  Key activities include:

Lead development oftheVOXZOGO global payer evidence strategy

Lead HEOR global and EMEA evidence generation,synthesis and disseminationin collaboration with other functions including Medical Affairs andBiometrics.

Support the reimbursement processes in the EMEA regionincludingsupport for the development of reimbursement dossiers and the adaption of economic models.


  • Plan, develop,synthesize and disseminate HEOR evidenceto demonstratethe value ofVOXZOGO
  • Coordinate theVOXZOGOGlobal Value and Access Team
  • Represent market access in global cross-functional forums including theData and Evidence Team and theGlobal Launch Team
  • Communicate market access perspective inclinical and observational study programs
  • Support EMEA reimbursement submissions with HEOR requirements
  • Continue innovation in approaches for HEOR in rare diseases


The scope of the role will part of the global HEOR Centre of Excellence and will comprise of planning and leading global HEORevidence generation within thehaemophilia franchise as well as providing support and expertiseto the regional and local market access teams as required.


  • Bachelor’s degree in relevant field (e.g. pharmacy, medical science, science)
  • Post graduate qualifications (Masters or PhD) in public health, health economics, epidemiology or statistics preferred


  • Minimum 8-10 years of HEOR experience obtained from either a consulting or pharmaceutical industry background
  • Sound knowledge and experience of differentpayer architypes and appreciation for thebroader market access environment ideallygainedacross multiple countries
  • Rare disease experience is preferred


No responsibility for supervision.


Liaising with internal market access, commercial, medical, clinical and regulatory departments and externally with the key decision makers, health economists, clinical experts and patient organizations.


  • Excellent verbal and written communication, collaboration, influence, strategic, analytical and problem-solving skills are required
  • Demonstrated ability to manage a range of HEOR evidence projects including cost-effectiveness models, budget impact models, systematic literature reviews andreal-world data analysis
  • Ability to provideinput into clinical program through input intotrial designs, statistical analysis plans and study reports
  • Demonstrated ability to gain alignment of stakeholders includinginternallyCommercial, Medical, Clinical and Regulatory departments and externallykey decision makers, health economists, clinical experts and patient organizations
  • Working knowledge of common statistical packages and reference management software would be an advantage.

Note:This description is not intendedto be all-inclusive or a limitation of the duties of the position.It is intended to describe the general nature of the job that may include other duties as assumed or assigned.

We are an equal opportunity employer and all qualified applicants will receive consideration for employment without regard to race, color, religion, gender, gender identity, sexual orientation, national origin, disability status, protected veteran status, or any other characteristic protected by law.

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We treat rare diseases, and that gives us rare opportunities. Chris Brodeur, Director, Corporate Compliance
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